DMD gene therapy (University of California)

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Report date: 2025/03/20 20:00:06

Base Information

Drug NameDMD gene therapy (University of California)
Drug Alias Namedystrophin gene therapy (University of California)
ClassificationCell and gene therapy > Gene therapy
Mechanisms of ActionDystrophin modulators
TargetsDystrophin
Therapy Area/IndicationsMuscular Dystrophies
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPending (Preclinical)
Highest Status in ChinaN/A
Originator CompaniesUniversity Of California
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Inactive CompaniesUniversity Of California
Active IndicationsN/A
Inactive IndicationsMuscular Dystrophies

Other Information

ATC CodeN/A
Related LinksN/A