Hurler syndrome gene therapy (Cincinnati Children's Hospital Medical Center/NINDS)

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Report date: 2026/01/27 10:14:04

Base Information

Drug NameHurler syndrome gene therapy (Cincinnati Children's Hospital Medical Center/NINDS)
Drug Alias NameN/A
ClassificationCell and gene therapy > Gene therapy
Mechanisms of ActionAlpha-L-iduronidase modulators
TargetsAlpha-L-iduronidase
Therapy Area/Indications +[1]  N/A
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPending (Preclinical)
Highest Status in ChinaN/A
Originator CompaniesCincinnati Children'S Hospital Medical Center
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Inactive CompaniesCincinnati Children'S Hospital Medical CenterNational Institute Of Neurological Disorders And Stroke
Active IndicationsN/A
Inactive Indications +[1]  N/A

Other Information

ATC CodeN/A
Related LinksN/A