Niemann Pick disease gene therapy (Genzyme)

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Report date: 2025/03/20 20:00:06

Base Information

Drug NameNiemann Pick disease gene therapy (Genzyme)
Drug Alias Namelysosomal storage disorders gene therapy (Genevo/Genzyme)lysosomal storage disorders gene therapy (Genzyme/Targeted Genetics)
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adenoviral vector
Mechanisms of ActionSphingomyelin phosphodiesterase stimulants
TargetsSphingomyelin phosphodiesterase
Therapy Area/IndicationsLysosomal Storage DiseasesNiemann-Pick Diseases
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusDiscontinued (Preclinical)
Highest Status in ChinaN/A
Originator CompaniesGenovo
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Inactive CompaniesGenzyme GeneralGenovoArmata Pharmaceuticals Inc
Active IndicationsN/A
Inactive IndicationsLysosomal Storage DiseasesNiemann-Pick Diseases

Other Information

ATC CodeN/A
Related LinksN/A