Rett Syndrome 1 gene therapy (University of Massachusetts/Sarepta)

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Report date: 2025/03/20 15:55:14

Base Information

Drug NameRett Syndrome 1 gene therapy (University of Massachusetts/Sarepta)
Drug Alias NameN/A
ClassificationCell and gene therapy > Gene therapy
Mechanisms of ActionNeuroprotectants
TargetsUpdating
Therapy Area/IndicationsRett Syndrome
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesSarepta Therapeutics Inc
China Registration ClassN/A

Develop Information

Active CompaniesSarepta Therapeutics IncUniversity of Massachusetts
Inactive CompaniesN/A
Active IndicationsRett Syndrome
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A