GFAP antisense oligonucleotide therapy (Ionis Pharmaceuticals/University Of Wisconsin-Madison)

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Report date: 2025/03/20 16:06:27
NME

Base Information

Drug NameGFAP antisense oligonucleotide therapy (Ionis Pharmaceuticals/University Of Wisconsin-Madison)
Drug Alias NameN/A
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide > Oligonucleotide antisense
Mechanisms of ActionGlial fibrillary acidic protein inhibitors
TargetsGlial fibrillary acidic protein
Therapy Area/IndicationsAlexander Disease
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited StatesEurope
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesIonis Pharmaceuticals Inc
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsAlexander Disease
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A