Niemann-Pick Type A disease therapeutics (Perlara)

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Report date: 2025/03/20 14:49:04
NME

Base Information

Drug NameNiemann-Pick Type A disease therapeutics (Perlara)
Drug Alias NameN/A
ClassificationSmall molecules > Heterocyclic drugs
Mechanisms of ActionSphingomyelin phosphodiesterase modulators
TargetsSphingomyelin phosphodiesterase
Therapy Area/IndicationsNiemann-Pick Disease, Type A
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesPerlara PBC
China Registration ClassN/A

Develop Information

Active CompaniesPerlara PBC
Inactive CompaniesN/A
Active IndicationsNiemann-Pick Disease, Type A
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A