modified SMN2 gene therapy (University of Western Australia)

N/A

Report date: 2025/03/20 20:00:06
NME

Base Information

Drug Namemodified SMN2 gene therapy (University of Western Australia)
Drug Alias NameN/A
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide > Oligonucleotide antisense
Mechanisms of ActionSMN2 gene modulators
TargetsUpdating
Therapy Area/IndicationsMuscular Atrophy, Spinal
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryAustralia and New Zealand
CombinationsNo
Global Highest StatusPending (Preclinical)
Highest Status in ChinaN/A
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Active IndicationsN/A
Inactive IndicationsMuscular Atrophy, Spinal

Other Information

ATC CodeN/A
Related LinksN/A