hammerhead ribozymes (Thomas Jefferson/Connecticut Universities)

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Report date: 2025/03/20 20:00:06
NME

Base Information

Drug Namehammerhead ribozymes (Thomas Jefferson/Connecticut Universities)
Drug Alias Namealpha1-AT modulator (Thomas Jefferson/Connecticut Universities)alpha1-AT expression modulator (Thomas Jefferson/Connecticut Universities)
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > RibozymeSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide
Mechanisms of ActionAlpha-1-antiproteinase modulators
TargetsAlpha-1-antiproteinase
Therapy Area/IndicationsEmphysemaLiver Diseases
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPending (Preclinical)
Highest Status in ChinaN/A
Originator CompaniesThomas Jefferson University
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Active IndicationsN/A
Inactive IndicationsEmphysemaLiver Diseases

Other Information

ATC CodeN/A
Related LinksN/A