mAb-conjugated GYS1-targeting siRNA (Avidity Biosciences)

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Report date: 2025/03/20 20:00:06

Base Information

Drug NamemAb-conjugated GYS1-targeting siRNA (Avidity Biosciences)
Drug Alias NameN/A
ClassificationBiologics > Protein drugs > Immunoglobulin > Antibody > Antibody conjugate > Monoclonal antibody conjugateBiologics > Protein drugs > Immunoglobulin > Antibody > Monoclonal antibody > Monoclonal antibody conjugate
Mechanisms of ActionTransferrin receptor protein 1 modulatorsGlycogen synthase 1 inhibitors
TargetsGlycogen synthase 1Transferrin receptor protein 1
Therapy Area/IndicationsGlycogen Storage Disease Type II
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusDiscontinued (Preclinical)
Highest Status in ChinaN/A
Originator CompaniesAvidity Biosciences Inc
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Inactive CompaniesAvidity Biosciences Inc
Active IndicationsN/A
Inactive IndicationsGlycogen Storage Disease Type II

Other Information

ATC CodeN/A
Related LinksN/A