maple syrup urine disease gene therapy (ASC Therapeutics/University of Massachusetts Medical School)

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Report date: 2025/03/20 16:09:35

Base Information

Drug Namemaple syrup urine disease gene therapy (ASC Therapeutics/University of Massachusetts Medical School)
Drug Alias NameAAV based gene therapy (ASC Therapeutics/Univ Massachusetts)adeno-associated virus based gene therapy (ASC Therapeutics/Univ Massachusetts)
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector
Mechanisms of ActionUpdating
TargetsUpdating
Therapy Area/IndicationsMaple Syrup Urine Disease
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesASC Therapeutics
China Registration ClassN/A

Develop Information

Active CompaniesUniversity Of Massachusetts Medical SchoolASC Therapeutics
Inactive CompaniesN/A
Active IndicationsMaple Syrup Urine Disease
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A