Ionis-AATRx

N/A

Report date: 2025/03/20 15:59:22
NME

Base Information

Drug NameIonis-AATRx
Drug Alias NameISIS-AATRx
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide > Oligonucleotide antisense
Mechanisms of ActionAlpha-1-antiproteinase inhibitors
TargetsAlpha-1-antiproteinase
Therapy Area/Indicationsalpha 1-Antitrypsin DeficiencyLiver Diseases
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPending (Preclinical)
Highest Status in ChinaN/A
Originator CompaniesIonis Pharmaceuticals Inc
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Active IndicationsN/A
Inactive Indicationsalpha 1-Antitrypsin DeficiencyLiver Diseases

Other Information

ATC CodeN/A
Related LinksN/A