Pip6a-PMO

N/A

Report date: 2025/04/21 17:03:46
NME

Base Information

Drug NamePip6a-PMO
Drug Alias NamePip6a-PMO
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide > Peptide-oligonucleotide ConjugateSmall molecules > Synthetic peptide > Peptide drug conjugate (PDC) > Peptide-oligonucleotide Conjugate
Mechanisms of ActionSMN gene transference
TargetsSurvival motor neuron protein
Therapy Area/IndicationsMuscular Atrophy, Spinal
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited Kingdom
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesUniversity Of Oxford
China Registration ClassN/A

Develop Information

Active CompaniesUniversity Of Oxford
Inactive CompaniesN/A
Active IndicationsMuscular Atrophy, Spinal
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A