oligonucleotide alpha-L-iduronidase (OPKO Health)

N/A

Report date: 2025/03/20 20:00:06
NME

Base Information

Drug Nameoligonucleotide alpha-L-iduronidase (OPKO Health)
Drug Alias NameN/A
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide
Mechanisms of ActionAlpha-L-iduronidase stimulants
TargetsAlpha-L-iduronidase
Therapy Area/IndicationsMucopolysaccharidosis I
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPending (Preclinical)
Highest Status in ChinaN/A
Originator CompaniesOpko Health Inc
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Inactive CompaniesOpko Health Inc
Active IndicationsN/A
Inactive IndicationsMucopolysaccharidosis I

Other Information

ATC CodeN/A
Related LinksN/A