oligonucleotide-based RNA therapeutics (AVI)

N/A

Report date: 2025/03/20 20:00:06
NME

Base Information

Drug Nameoligonucleotide-based RNA therapeutics (AVI)
Drug Alias Nameexon-skipping pre-RNAi therapeutics (AVI)
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide > Oligonucleotide antisense
Mechanisms of ActionHemoglobin beta chain modulators
TargetsHemoglobin beta chain
Therapy Area/IndicationsThalassemia
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusDiscontinued (Preclinical)
Highest Status in ChinaN/A
Originator CompaniesErcole Biotech Inc
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Inactive CompaniesErcole Biotech IncSarepta Therapeutics Inc
Active IndicationsN/A
Inactive IndicationsThalassemia

Other Information

ATC CodeN/A
Related LinksN/A