SMN enhancing small molecules (California Institute for Biomedical Research/Families of Spinal Muscular Atrophy)

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Report date: 2025/03/20 20:00:06
NME

Base Information

Drug NameSMN enhancing small molecules (California Institute for Biomedical Research/Families of Spinal Muscular Atrophy)
Drug Alias NameSMN enhancing small molecules (CALIBR/Families of SMA)
ClassificationSmall molecules > Heterocyclic drugs
Mechanisms of ActionSurvival motor neuron protein stimulants
TargetsSurvival motor neuron protein
Therapy Area/IndicationsMuscular Atrophy, Spinal
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPending (Preclinical)
Highest Status in ChinaN/A
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Active IndicationsN/A
Inactive IndicationsMuscular Atrophy, Spinal

Other Information

ATC CodeN/A
Related LinksN/A