SMN1 gene modulator (Genea Biocells)

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Report date: 2025/03/20 09:44:49
NME

Base Information

Drug NameSMN1 gene modulator (Genea Biocells)
Drug Alias Namesmall molecule therapeutics (Genea Biocells)
ClassificationSmall molecules > Heterocyclic drugs
Mechanisms of ActionSurvival motor neuron protein modulators
TargetsSurvival motor neuron protein
Therapy Area/IndicationsMuscular Atrophy, Spinal
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesGenea Biocells US Inc
China Registration ClassN/A

Develop Information

Active CompaniesGenea Biocells US Inc
Inactive CompaniesN/A
Active IndicationsMuscular Atrophy, Spinal
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A