SMN2 upregulating program (Translate Bio)

N/A

Report date: 2025/03/20 20:00:06
NME

Base Information

Drug NameSMN2 upregulating program (Translate Bio)
Drug Alias NameSMN2 upregulating program (RaNA Therapeutics)
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide
Mechanisms of ActionSMN2 gene stimulants
TargetsUpdating
Therapy Area/IndicationsMuscular Atrophy, Spinal
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPending (Preclinical)
Highest Status in ChinaN/A
Originator CompaniesTranslate Bio Ma Inc
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Inactive CompaniesTranslate Bio Ma Inc
Active IndicationsN/A
Inactive IndicationsMuscular Atrophy, Spinal

Other Information

ATC CodeN/A
Related LinksN/A