antisense oligonucleotides (Ionis/Genzyme)

N/A

Report date: 2025/06/11 20:01:15
NME

Base Information

Drug Nameantisense oligonucleotides (Ionis/Genzyme)
Drug Alias Nameantisense huntingtin expression inhibitors (Isis/Genzyme)antisense oligonucleotides (Isis/Genzyme)ISIS-387898ISIS-436689ISIS-388241 +[6
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide > Oligonucleotide antisense
Mechanisms of ActionHuntingtin inhibitorsAntisense oligonucleotide inhibitors
TargetsHuntingtin
Therapy Area/IndicationsHuntington Disease
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPending (Preclinical)
Highest Status in ChinaN/A
Originator CompaniesIonis Pharmaceuticals Inc
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Active IndicationsN/A
Inactive IndicationsHuntington Disease

Other Information

ATC CodeN/A
Related LinksN/A