antisense oligonucleotides (Ionis/University of Utah)

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Report date: 2025/06/11 10:24:46
NME

Base Information

Drug Nameantisense oligonucleotides (Ionis/University of Utah)
Drug Alias Nameantisense oligonucleotides (Isis Pharmaceuticals/University of Utah)ASO-1ASO-3ASO-5ASO-7
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide > Oligonucleotide antisense
Mechanisms of ActionAntisense oligonucleotide inhibitorsAtaxin-2 inhibitors
TargetsAtaxin-2
Therapy Area/IndicationsSpinocerebellar Ataxias
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesIonis Pharmaceuticals Inc
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsSpinocerebellar Ataxias
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A