Non-aminoglycoside stop codon suppressors (UCLA)

N/A

Report date: 2025/06/11 20:01:15
NME

Base Information

Drug NameNon-aminoglycoside stop codon suppressors (UCLA)
Drug Alias NameBZ-22BZ-9BZ-16BZ-6RTC-13 +[6
ClassificationSmall molecules
Mechanisms of ActionDystrophin expression stimulantsNeuroprotectants
TargetsDystrophin
Therapy Area/IndicationsAtaxia TelangiectasiaMuscular Dystrophy, Duchenne
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPending (Preclinical)
Highest Status in ChinaN/A
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Active IndicationsN/A
Inactive IndicationsAtaxia TelangiectasiaMuscular Dystrophy, Duchenne

Other Information

ATC CodeN/A
Related LinksN/A