AAV8 vectors encoding nanobodies (INSERM)

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Report date: 2025/06/11 11:01:40

Base Information

Drug NameAAV8 vectors encoding nanobodies (INSERM)
Drug Alias NameKB-AT-02/03AAV8-AT 02/03AAV8-AT-113KB-AT-113
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector
Mechanisms of ActionCoagulation factor VIII stimulantsCoagulation factor IX stimulants
TargetsCoagulation factor VIIICoagulation factor IX
Therapy Area/IndicationsHemophilia BHemophilia A
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryFrance
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesGenethon
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsHemophilia BHemophilia A
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A