Small molecules program (Vertex Pharmaceuticals)

N/A

Report date: 2025/12/25 10:09:48
NME

Base Information

Drug NameSmall molecules program (Vertex Pharmaceuticals)
Drug Alias NameAlpha-1 antitrypsin deficiency therapy (Vertex Pharmaceuticals)
ClassificationSmall molecules
Mechanisms of ActionUpdating
TargetsUpdating
Therapy Area/Indicationsalpha 1-Antitrypsin Deficiency
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesVertex Pharmaceuticals Gmbh
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active Indicationsalpha 1-Antitrypsin Deficiency
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A