GA-003 (Genosera)

N/A

Report date: 2025/06/11 10:52:51

Base Information

Drug NameGA-003 (Genosera)
Drug Alias NameFKRP gene therapy (Genosera)
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector
Mechanisms of ActionRibitol 5-phosphate transferase FKRP gene transference
TargetsRibitol 5-phosphate transferase FKRP
Therapy Area/IndicationsMuscular Dystrophies, Limb-Girdle
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesGenosera Inc
China Registration ClassN/A

Develop Information

Active CompaniesGenosera Inc
Inactive CompaniesN/A
Active IndicationsMuscular Dystrophies, Limb-Girdle
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A