nonsense suppression therapy (PTC therapeutics/University of Alabama)

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Report date: 2025/06/11 20:01:15
NME

Base Information

Drug Namenonsense suppression therapy (PTC therapeutics/University of Alabama)
Drug Alias NamePTC-415PTC-418
ClassificationSmall molecules
Mechanisms of ActionAlpha-L-iduronidase stimulants
TargetsAlpha-L-iduronidase
Therapy Area/IndicationsMucopolysaccharidosis I
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPending (Preclinical)
Highest Status in ChinaN/A
Originator CompaniesPtc Therapeutics Inc
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Inactive CompaniesPtc Therapeutics IncUniversity Of Alabama At Birmingham
Active IndicationsN/A
Inactive IndicationsMucopolysaccharidosis I

Other Information

ATC CodeN/A
Related LinksN/A