adeno-associated virus based Factor VIII gene therapy (Asklepios BioPharmaceutical/University of Carolina)

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Report date: 2025/06/11 10:30:41

Base Information

Drug Nameadeno-associated virus based Factor VIII gene therapy (Asklepios BioPharmaceutical/University of Carolina)
Drug Alias NameN/A
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector
Mechanisms of ActionCoagulation factor VIII stimulants
TargetsCoagulation factor VIII
Therapy Area/IndicationsHemophilia A
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesUnc
China Registration ClassN/A

Develop Information

Active CompaniesAskBio IncUnc
Inactive CompaniesN/A
Active IndicationsHemophilia A
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A