Adeno-associated viral vector serotype 9 containing the human MECP2 gene (Transcrip Ireland)

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Report date: 2025/06/11 10:50:25

Base Information

Drug NameAdeno-associated viral vector serotype 9 containing the human MECP2 gene (Transcrip Ireland)
Drug Alias NameMECP2 gene therapy (Transcrip Ireland)
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector
Mechanisms of ActionMethyl-CpG-binding protein 2 modulators
TargetsMethyl-CpG-binding protein 2
Therapy Area/IndicationsRett Syndrome
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryEurope
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesTranscrip Ireland Ltd
China Registration ClassN/A

Develop Information

Active CompaniesTranscrip Ireland Ltd
Inactive CompaniesN/A
Active IndicationsRett Syndrome
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A