ETX-201 (Encoded)

N/A

Report date: 2026/05/06 20:02:28

Base Information

Drug NameETX-201 (Encoded)

Drug Alias NameAAV9-miRNA (Encoded Therapeutics)UBE3A-ATS miRNA therapy (Encoded Therapeutics)ETX-201

ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide > microRNACell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector

Mechanisms of ActionNeuroprotectantsUbiquitin-like modifier-activating enzyme 3A modulators

TargetsUbiquitin-like modifier-activating enzyme 3A

Therapy Area/IndicationsAngelman Syndrome

Global Approved IndicationsN/A

Approved Indications in ChinaN/A

Original Approved Country/TerritoryN/A

Original Approved DateN/A

Country/TerritoryUnited States

CombinationsNo

Global Highest StatusPreclinical

Highest Status in ChinaN/A

Originator CompaniesEncoded Therapeutics Inc

China Registration ClassN/A

Develop Information

Active CompaniesEncoded Therapeutics Inc

Inactive CompaniesN/A

Active IndicationsAngelman Syndrome

Inactive IndicationsN/A

Other Information

ATC CodeN/A