Exosome-mediated arginase 1 enzyme replacement therapy (Capricor Therapeutics)

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Report date: 2026/01/27 16:11:05

Base Information

Drug NameExosome-mediated arginase 1 enzyme replacement therapy (Capricor Therapeutics)
Drug Alias NameArg1 gene therapy (Capricor Therapeutics)
ClassificationBiologics > ExosomesCell and gene therapy > Gene therapy
Mechanisms of ActionArginase-1 stimulants
TargetsArginase-1
Therapy Area/IndicationsHyperargininemia
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesCapricor Therapeutics Inc
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsHyperargininemia
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A