SMN1 gene therapy (Skyline Therapeutics)

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Report date: 2025/06/11 11:07:27

Base Information

Drug NameSMN1 gene therapy (Skyline Therapeutics)
Drug Alias Nameadeno-associated virus delivered SMN1 gene therapy (Skyline therapeutics)SKG-1201
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector
Mechanisms of ActionSurvival motor neuron protein stimulants
TargetsSurvival motor neuron protein
Therapy Area/IndicationsMuscular Atrophy, Spinal
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryMainland China
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaPreclinical
Originator CompaniesSkyline Therapeutics (Shanghai) Co Ltd
China Registration ClassN/A

Develop Information

Active CompaniesSkyline Therapeutics (Shanghai) Co Ltd
Inactive CompaniesN/A
Active IndicationsMuscular Atrophy, Spinal
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A