STXBP1-RD program (Encoded Therapeutics)

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Report date: 2025/06/11 10:53:58

Base Information

Drug NameSTXBP1-RD program (Encoded Therapeutics)
Drug Alias NameSTXBP1 gene therapy (Encoded Therapeutics)
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector
Mechanisms of ActionNeuroprotectantsSyntaxin-binding protein 1 gene transference
TargetsSyntaxin-binding protein 1
Therapy Area/IndicationsCentral Nervous System Diseases
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesEncoded Therapeutics Inc
China Registration ClassN/A

Develop Information

Active CompaniesEncoded Therapeutics Inc
Inactive CompaniesN/A
Active IndicationsCentral Nervous System Diseases
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A