ABCA4 gene therapy (SpliceBio)

N/A

Report date: 2025/06/11 10:54:03

Base Information

Drug NameABCA4 gene therapy (SpliceBio)
Drug Alias NameN/A
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector
Mechanisms of ActionRetinal-specific phospholipid-transporting ATPase ABCA4 modulators
TargetsRetinal-specific phospholipid-transporting ATPase ABCA4
Therapy Area/IndicationsRetinal Dysplasia
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesSpliceBio SL
China Registration ClassN/A

Develop Information

Active CompaniesSpliceBio SL
Inactive CompaniesN/A
Active IndicationsRetinal Dysplasia
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A