Autologous hematopoietic stem cells and progenitor cells (Fondazione Telethon Ets)

N/A

Report date: 2026/05/20 20:02:01

Base Information

Drug NameAutologous hematopoietic stem cells and progenitor cells (Fondazione Telethon Ets)

Drug Alias NameN/A

ClassificationCell and gene therapy > Cell therapy > Stem cell therapy > Hematopoietic stem cells therapyCell and gene therapy > Cell therapy > Donor > AutologousCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Retroviral vector

Mechanisms of ActionBeta-galactosidase modulatorsHematopoietic progenitor cell antigen CD34 modulators

TargetsBeta-galactosidaseHematopoietic progenitor cell antigen CD34

Therapy Area/IndicationsMucopolysaccharidosis IValpha-MannosidosisGangliosidosis, GM1

Global Approved IndicationsN/A

Approved Indications in ChinaN/A

Original Approved Country/TerritoryN/A

Original Approved DateN/A

Country/TerritoryItaly

CombinationsNo

Global Highest StatusPreclinical

Highest Status in ChinaN/A

Originator CompaniesFondazione Telethon

China Registration ClassN/A

Develop Information

Active CompaniesFondazione Telethon

Inactive CompaniesN/A

Active IndicationsMucopolysaccharidosis IValpha-MannosidosisGangliosidosis, GM1

Inactive IndicationsN/A

Other Information

ATC CodeN/A