ANO5 gene replacement therapy (Cure Rare Disease/LGMD2L Foundation)

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Report date: 2026/05/20 20:02:01

Base Information

Drug NameANO5 gene replacement therapy (Cure Rare Disease/LGMD2L Foundation)
Drug Alias NameN/A
ClassificationBiologics
Mechanisms of ActionAnoctamin-5 modulators
TargetsAnoctamin-5
Therapy Area/IndicationsMuscular Dystrophies, Limb-Girdle
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesCure Rare Disease
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsMuscular Dystrophies, Limb-Girdle
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A