AMT-080

N/A

Report date: 2023/10/26 16:41:01

Base Information

Drug NameAMT-080
Drug Alias NameAAV-gene therapy (AMT)Exon-skipping dystrophin gene therapy (AMT)AMT-080
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector
Mechanisms of ActionDystrophin pre-mRNA stimulants
TargetsDystrophin pre-mRNA
Therapy Area/IndicationsMuscular Dystrophy, Duchenne
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryN/A
CombinationsNo
Global Highest StatusPending (Preclinical)
Highest Status in ChinaN/A
Originator CompaniesAmsterdam Molecular TherapeuticsUniqure Biopharma Bv
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Inactive CompaniesUniqureAmsterdam Molecular Therapeutics
Active IndicationsN/A
Inactive IndicationsMuscular Dystrophy, Duchenne

Other Information

ATC CodeN/A
Related LinksN/A