AAV1-gamma-sarcoglycan vector(Genethon)

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Report date: 2023/10/26 16:40:53

Base Information

Drug NameAAV1-gamma-sarcoglycan vector(Genethon)
Drug Alias NameGamma sarcoglycanopathy gene therapyAdeno-associated viral 1 vector-mediated gamma-sarcoglycan gene therapyAdeno-associated virus 1-gamma-sarcoglycan gene therapyAAV1-gamma-sarcoglycan gene therapy - GenethonAAV1-gamma-sarcoglycan vector injection +[7
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector
Mechanisms of ActionGamma-sarcoglycan gene transference
TargetsGamma-sarcoglycan
Therapy Area/IndicationsMuscular Dystrophies, Limb-Girdle
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryN/A
CombinationsNo
Global Highest StatusPhase 1 Clinical
Highest Status in ChinaN/A
Originator CompaniesViromed
China Registration ClassN/A

Develop Information

Active CompaniesViromedGenethon
Inactive CompaniesN/A
Active IndicationsMuscular Dystrophies, Limb-Girdle
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A