Sapablursen

N/A

Report date: 2026/05/09 20:00:18
NME

Base Information

Drug NameSapablursen
Drug Alias NameIONIS TMPRSS6-LrxISIS-702843
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide > Oligonucleotide antisense
Mechanisms of ActionTransmembrane protease serine 6 inhibitors
TargetsTransmembrane protease serine 6
Therapy Area/Indicationsbeta-ThalassemiaThalassemiaPolycythemia Vera
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited StatesThailandTurkey +[6
CombinationsNo
Global Highest StatusPhase 3 Clinical
Highest Status in ChinaN/A
Originator CompaniesIonis Pharmaceuticals Inc
China Registration ClassN/A

Develop Information

Inactive CompaniesIonis Pharmaceuticals Inc
Active IndicationsPolycythemia Vera
Inactive Indicationsbeta-ThalassemiaThalassemia

Other Information

ATC CodeN/A
Related LinksN/A