Ultevursen

N/A

Report date: 2026/02/07 20:00:33

Base Information

Drug NameUltevursen
Drug Alias NameQR-421aQR-421-a
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide > Oligonucleotide antisense
Mechanisms of ActionRNA interferenceUsherin expression inhibitors
TargetsUsherin
Therapy Area/IndicationsRetinal DiseasesRetinitis PigmentosaEye Diseases, Hereditary +[8] 
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryBelgiumCanadaUnited States +[10] 
CombinationsNo
Global Highest StatusPhase 2 Clinical
Highest Status in ChinaN/A
Originator CompaniesProqr Therapeutics
China Registration ClassN/A

Develop Information

Active CompaniesSepul BioProqr TherapeuticsLaboratoires Thea SAS
Inactive CompaniesN/A
Active IndicationsRetinal DiseasesRetinitis PigmentosaEye Diseases, Hereditary +[7] 
Inactive IndicationsEye Diseases

Other Information

ATC CodeN/A
Related LinksN/A