Adeno-virus gene therapy (Applied Genetic Technologies Corporation)

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Report date: 2023/10/26 16:21:35

Base Information

Drug NameAdeno-virus gene therapy (Applied Genetic Technologies Corporation)
Drug Alias NameN/A
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adenoviral vector
Mechanisms of ActionMT-ND4 gene transference
TargetsNADH-ubiquinone oxidoreductase chain 4
Therapy Area/IndicationsOptic Atrophy, Hereditary, Leber
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryN/A
CombinationsNo
Global Highest StatusDiscontinued (Phase 2 Clinical)
Highest Status in ChinaN/A
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Active IndicationsN/A
Inactive IndicationsOptic Atrophy, Hereditary, Leber

Other Information

ATC CodeN/A
Related LinksN/A