EXG-34217

N/A

Report date: 2026/02/07 20:00:33

Base Information

Drug NameEXG-34217
Drug Alias NameEXG-34217
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > SeV vector
Mechanisms of ActionZinc finger and SCAN domain-containing protein 4 gene transference
TargetsZinc finger and SCAN domain-containing protein 4
Therapy Area/IndicationsTelomere ShorteningBone Marrow Failure Disorders
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPhase 2 Clinical
Highest Status in ChinaN/A
Originator CompaniesElixirgen
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsTelomere ShorteningBone Marrow Failure Disorders
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A