AVR-RD-04

N/A

Report date: 2025/03/12 13:46:09

Base Information

Drug NameAVR-RD-04
Drug Alias NameAVR-RD-04CTNS-RD-04AVR-RD-O4
ClassificationCell and gene therapy > Cell therapy > Donor > AutologousCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Lentiviral vectorCell and gene therapy > Cell therapy > Stem cell therapy > Hematopoietic stem cells therapy +[4] 
Mechanisms of ActionCTNS gene stimulants
TargetsCystinosin
Therapy Area/IndicationsCystinosisLysosomal Storage Diseases
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPhase 2 Clinical
Highest Status in ChinaN/A
Originator CompaniesGenStem Therapeutics Inc
China Registration ClassN/A

Develop Information

Active CompaniesAvrobio IncAvrobioNovartis Pharma Ag +[4] 
Inactive CompaniesN/A
Active IndicationsCystinosisLysosomal Storage Diseases
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A