Exaluren

N/A

Report date: 2026/04/14 20:00:15
NME

Base Information

Drug NameExaluren
Drug Alias NameSynthetic aminoglycosideELX-02NB-124
ClassificationSmall molecules > Heterocyclic drugs > Antibiotics > Aminoglycoside antibiotics
Mechanisms of ActionSmall Ribosome subunits modulators
TargetsSmall Ribosome subunits
Therapy Area/IndicationsCystinosisGenetic Diseases, X-LinkedGenetic Diseases, Inborn +[6
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryBelgiumCanadaUnited States +[7
CombinationsNo
Global Highest StatusPhase 2 Clinical
Highest Status in ChinaN/A
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsGenetic Diseases, X-LinkedNephritis, HereditaryCystic Fibrosis
Inactive IndicationsCystinosisGenetic Diseases, InbornRenal Insufficiency

Other Information

ATC CodeN/A
Related LinksDrugBank