AAV1-FS344

N/A

Report date: 2023/10/26 16:20:54

Base Information

Drug NameAAV1-FS344
Drug Alias NamerAAV1.CMV.huFollistin344rAAV1 CMV huFollistatin 344Gene therapy-delivered myostatin inhibitorAAV1.CMV.huFS344AAV1-Follistatin +[6] 
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector > AAV1 vector
Mechanisms of ActionGene transferenceGrowth/differentiation factor 8 inhibitorsFollistatin agonists
TargetsFollistatinGrowth/differentiation factor 8
Therapy Area/IndicationsBecker muscular dystrophyMyositis, Inclusion BodyMuscular Dystrophy, Duchenne
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPhase 2 Clinical
Highest Status in ChinaN/A
Originator CompaniesNationwide Children'S Hospital
China Registration ClassN/A

Develop Information

Active CompaniesMilo BiotechnologyNationwide Children'S Hospital
Inactive CompaniesN/A
Active IndicationsMyositis, Inclusion BodyMuscular Dystrophy, Duchenne
Inactive IndicationsBecker muscular dystrophy

Other Information

ATC CodeN/A
Related LinksN/A