Cystic fibrosis gene therapy

N/A

Report date: 2022/01/14 13:23:58

Base Information

Drug NameCystic fibrosis gene therapy
Drug Alias NameDNA nanoparticle gene therapy囊性纤维化基因治疗Plasmid DNA vector expressing cystic fibrosis transmembrane geneCompacted DNA
ClassificationCell and gene therapy > Gene therapy > Plasmid
Mechanisms of ActionCystic fibrosis transmembrane conductance regulator stimulants
TargetsCystic fibrosis transmembrane conductance regulator
Therapy Area/IndicationsCystic Fibrosis
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryN/A
CombinationsNo
Global Highest StatusPending (Phase 2 Clinical)
Highest Status in ChinaN/A
Originator CompaniesCopernicus Therapeutics
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Inactive CompaniesCopernicus Therapeutics
Active IndicationsN/A
Inactive IndicationsCystic Fibrosis

Other Information

ATC CodeN/A
Related LinksN/A