AAVrh.10CUCLN2 (Weill Medical College of Cornell University)

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Report date: 2023/10/26 16:20:29

Base Information

Drug NameAAVrh.10CUCLN2 (Weill Medical College of Cornell University)
Drug Alias NameN/A
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector > AAVrh10 vector
Mechanisms of ActionCLN2 gene transference
TargetsCeroid-lipofuscinosis neuronal protein 2
Therapy Area/IndicationsNeuronal Ceroid-Lipofuscinoses
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPhase 2 Clinical
Highest Status in ChinaN/A
Originator CompaniesWeill Cornell Medical College
China Registration ClassN/A

Develop Information

Active IndicationsNeuronal Ceroid-Lipofuscinoses
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A