Rusfertide

N/A

Report date: 2026/03/09 20:02:04
NMEFirst In Class

Base Information

Drug NameRusfertide
Drug Alias NamePTG-300
ClassificationSmall molecules > Synthetic peptide
Mechanisms of ActionHepcidin replacements
TargetsNot applicable
Therapy Area/IndicationsHemochromatosisbeta-ThalassemiaAnemia, Hemolytic +[4
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryCzechiaBelgiumCanada +[27
CombinationsNo
Global Highest StatusNDA/BLA
Highest Status in ChinaN/A
Originator CompaniesProtagonist Therapeutics Inc
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsHemochromatosisPolycythemia Vera
Inactive Indicationsbeta-ThalassemiaAnemia, Hemolytic

Other Information

ATC CodeN/A
Related LinksN/A