Adeno-associated viral vector expressing human retinoschisin-1 gene therapy

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Report date: 2023/10/26 16:19:45

Base Information

Drug NameAdeno-associated viral vector expressing human retinoschisin-1 gene therapy
Drug Alias NameXLRS gene therapyRS1 AAV vectorrAAV2tYF CB hRS1rAAV hRS1rAAV2tYF-CB-hRS1
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector > AAV2 vector
Mechanisms of ActionRetinoschisin stimulantsGene transference
TargetsRetinoschisin
Therapy Area/IndicationsRetinoschisis
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited StatesMainland China
CombinationsNo
Global Highest StatusPhase 2 Clinical
Highest Status in ChinaPhase 1 Clinical
Originator CompaniesApplied Genetic
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsRetinoschisis
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A