Triheptanoin

N/A

Report date: 2026/04/22 20:01:10
NME

Base Information

Drug NameTriheptanoin
Drug Alias NameGlycerol triheptanoate三庚酸甘油酯三庚精Glyceryl triheptanoate三庚酸甘油脂 +[10] 
ClassificationSmall molecules > Heterocyclic drugs
Mechanisms of ActionFatty acid replacementsTriglyceride replacements
TargetsNot applicable
Therapy Area/IndicationsGlucose transporter type 1 deficiency syndromePolyglucosan Body Disease, Adult FormLipid Metabolism Disorders +[20] 
Global Approved IndicationsLipid Metabolism Disorders
Approved Indications in ChinaN/A
Original Approved Country/TerritoryUnited States
Original Approved Date2020/06/30
Country/TerritoryCzechiaCanadaUnited States +[15] 
CombinationsNo
Global Highest StatusApproved
Highest Status in ChinaN/A
Originator CompaniesBaylor Research Institute Llc
China Registration ClassN/A

Develop Information

Active CompaniesUniversity of Texas Southwestern Medical CenterUltragenyx Pharmaceutical IncBaylor Research Institute Llc
Inactive CompaniesInstitut National De La Santé Et De La Recherche Médicale, France U979University of LiegeOregon Health And Science University +[5] 
Active IndicationsGlucose transporter type 1 deficiency syndromeLipid Metabolism DisordersGlucose Metabolism Disorders +[7] 
Inactive IndicationsPolyglucosan Body Disease, Adult FormGlycogen Storage Disease Type VGlycogen Storage Disease Type IV +[13] 

Other Information

ATC CodeA
Related LinksWikipediaDrugBankKEGG