GNT-0003

N/A

Report date: 2024/12/13 16:15:50

Base Information

Drug NameGNT-0003
Drug Alias NamerAAV8-hUGT1A1Adeno-associated Viral Vector expressing UGT1A1 transgeneGNT-0003
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector > AAV8 vector
Mechanisms of ActionGene transferenceUGT1A1 enzyme replacements
TargetsUDP-glucuronosyltransferase 1-1
Therapy Area/IndicationsCrigler-Najjar Syndrome
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryFrance
CombinationsNo
Global Highest StatusPhase 2 Clinical
Highest Status in ChinaN/A
Originator CompaniesGenethon
China Registration ClassN/A

Develop Information

Active CompaniesGenethon
Inactive CompaniesN/A
Active IndicationsCrigler-Najjar Syndrome
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A