Lucerastat

芦舍司他

Report date: 2024/12/20 14:49:35
NME

Base Information

Drug NameLucerastat
Drug Alias Name卢雷司他lucerastatumN-ButylgalactonojirimycinN-ButyldeoxygalactonojirimycinACT-434964 +[9
ClassificationSmall molecules > Heterocyclic drugs
Mechanisms of ActionCeramide glucosyltransferase inhibitors
TargetsCeramide glucosyltransferase
Therapy Area/IndicationsFabry Disease
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryBelgiumCanadaUnited States +[15
CombinationsNo
Global Highest StatusPhase 3 Clinical
Highest Status in ChinaN/A
Originator CompaniesActelion Pharmaceuticals Ltd
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsFabry Disease
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A