tgAAV-CF gene therapy (Targeted Genetics)

N/A

Report date: 2023/10/26 16:02:25

Base Information

Drug NametgAAV-CF gene therapy (Targeted Genetics)
Drug Alias NametgAAVCFtgAAV2-CF
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector > AAV2 vector
Mechanisms of ActionCystic fibrosis transmembrane conductance regulator inhibitors
TargetsCystic fibrosis transmembrane conductance regulator
Therapy Area/IndicationsCystic Fibrosis
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryN/A
CombinationsNo
Global Highest StatusDiscontinued (Phase 2 Clinical)
Highest Status in ChinaN/A
Originator CompaniesTargeted Genetics
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Inactive CompaniesTargeted Genetics
Active IndicationsN/A
Inactive IndicationsCystic Fibrosis

Other Information

ATC CodeN/A
Related LinksN/A